罕见病领域研究现状与趋势分析
贺彩红, 蒋琬姿, 张丽雯, 阮梅花, 周红文, 于建荣

Current status and future perspectives of rare disease research
He Caihong, Jiang Wanzi, Zhang Liwen, Ruan Meihua, Zhou Hongwen, Yu Jianrong
图13 药物数量排名前20位的靶标作用机制
Fig. 13 Top 20 target-based actions for rare diseases